Target selection by natural and redesigned PUF proteins

Edited by Roy Parker, University of Colorado, Boulder, CO, and approved November 12, 2015 (received for review April 30, 2015)
December 14, 2015
112 (52) 15868-15873

Significance

Pumilio/fem-3 mRNA binding factor (PUF) proteins have become a leading scaffold in designing proteins to bind and control RNAs at will. We analyze the effects of that reengineering across the transcriptome in vivo for the first time to our knowledge. We show that yeast Puf2p, a noncanonical PUF protein, binds more than 1,000 mRNA targets. Puf2p binds multiple UAAU elements, unlike canonical PUF proteins. We design a modified Puf2p to bind UAAG rather than UAAU, which allows us to align the protein with the binding site. In vivo, the redesigned protein binds UAAG sites. Its altered specificity redistributes the protein away from 3′UTRs, such that the protein tracks with its sites, binds throughout the mRNA and represses a novel RNA network.

Abstract

Pumilio/fem-3 mRNA binding factor (PUF) proteins bind RNA with sequence specificity and modularity, and have become exemplary scaffolds in the reengineering of new RNA specificities. Here, we report the in vivo RNA binding sites of wild-type (WT) and reengineered forms of the PUF protein Saccharomyces cerevisiae Puf2p across the transcriptome. Puf2p defines an ancient protein family present throughout fungi, with divergent and distinctive PUF RNA binding domains, RNA-recognition motifs (RRMs), and prion regions. We identify sites in RNA bound to Puf2p in vivo by using two forms of UV cross-linking followed by immunopurification. The protein specifically binds more than 1,000 mRNAs, which contain multiple iterations of UAAU-binding elements. Regions outside the PUF domain, including the RRM, enhance discrimination among targets. Compensatory mutants reveal that one Puf2p molecule binds one UAAU sequence, and align the protein with the RNA site. Based on this architecture, we redesign Puf2p to bind UAAG and identify the targets of this reengineered PUF in vivo. The mutant protein finds its target site in 1,800 RNAs and yields a novel RNA network with a dramatic redistribution of binding elements. The mutant protein exhibits even greater RNA specificity than wild type. The redesigned protein decreases the abundance of RNAs in its redesigned network. These results suggest that reengineering using the PUF scaffold redirects and can even enhance specificity in vivo.

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Data Availability

Data deposition: The data reported in this paper have been deposited in the Gene Expression Omnibus (GEO) database, www.ncbi.nlm.nih.gov/geo (accession no. GSE73274).

Acknowledgments

We thank M. Preston, C. Lapointe, A. Prasad, E. Sorokin, and B. Carrick for comments; L. Vanderploeg for assistance in figure preparation; and the University of Wisconsin Biotechnology Center DNA Sequencing Facility for assistance with performing RNA-seq. This work was supported by a gift from D.F.P., and NIH Grants R01 GM050942 (to M.W.) and T32 GM008349 (to D.F.P.). The synthesis of 4-thiouridine was supported by NIH Grant R01 CA073808 (to R.T.R.) and Canadian Institutes of Health Research (CIHR) Grant 289613 (to B.V.).

Supporting Information

Appendix (PDF)
Supporting Information
pnas.1508501112.sd01.xls
pnas.1508501112.sd02.xls
pnas.1508501112.sd03.xls

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Information & Authors

Information

Published in

The cover image for PNAS Vol.112; No.52
Proceedings of the National Academy of Sciences
Vol. 112 | No. 52
December 29, 2015
PubMed: 26668354

Classifications

Data Availability

Data deposition: The data reported in this paper have been deposited in the Gene Expression Omnibus (GEO) database, www.ncbi.nlm.nih.gov/geo (accession no. GSE73274).

Submission history

Published online: December 14, 2015
Published in issue: December 29, 2015

Keywords

  1. PUF proteins
  2. RNA-binding proteins
  3. synthetic biology
  4. designer protein
  5. CLIP-seq

Acknowledgments

We thank M. Preston, C. Lapointe, A. Prasad, E. Sorokin, and B. Carrick for comments; L. Vanderploeg for assistance in figure preparation; and the University of Wisconsin Biotechnology Center DNA Sequencing Facility for assistance with performing RNA-seq. This work was supported by a gift from D.F.P., and NIH Grants R01 GM050942 (to M.W.) and T32 GM008349 (to D.F.P.). The synthesis of 4-thiouridine was supported by NIH Grant R01 CA073808 (to R.T.R.) and Canadian Institutes of Health Research (CIHR) Grant 289613 (to B.V.).

Notes

This article is a PNAS Direct Submission.

Authors

Affiliations

Douglas F. Porter
Department of Biochemistry, University of Wisconsin, Madison, WI 53706;
Biotechnology Training Program, University of Wisconsin, Madison, WI 53706;
Yvonne Y. Koh
The Biofactory Pte Ltd, 40856, Singapore;
Brett VanVeller
Department of Chemistry, Iowa State University, Ames, IA 50011;
Ronald T. Raines
Department of Biochemistry, University of Wisconsin, Madison, WI 53706;
Department of Chemistry, University of Wisconsin, Madison, WI 53706
Marvin Wickens1 [email protected]
Department of Biochemistry, University of Wisconsin, Madison, WI 53706;

Notes

1
To whom correspondence should be addressed. Email: [email protected].
Author contributions: D.F.P., Y.Y.K., B.V., R.T.R., and M.W. designed research; D.F.P., Y.Y.K., and B.V. performed research; D.F.P. contributed new reagents/analytic tools; D.F.P., Y.Y.K., B.V., and M.W. analyzed data; and D.F.P., B.V., R.T.R., and M.W. wrote the paper.

Competing Interests

The authors declare no conflict of interest.

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    Target selection by natural and redesigned PUF proteins
    Proceedings of the National Academy of Sciences
    • Vol. 112
    • No. 52
    • pp. 15767-E7307

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